Hope for Teen With Rare Illness
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Progeria is an extremely rare disease that afflicts about 200 kids in the world. But there's some hope for one teen who's participating in a new drug trial. The disease causes rapid aging, a decrease in bone and muscle density, and increases the risk of stroke and heart attack in the children who are born with it. The average age of death for these children is 13 years old. This boy is now 16 year old.

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Hope for Teen With Rare Illness - as part of the news series by GeoBeats. Progeria is an extremely rare disease that afflicts about 200 kids in the world. But there's some hope for one teen who's participating in a new drug trial. The disease causes rapid aging, a decrease in bone and muscle density, and increases the risk of stroke and heart attack in the children who are born with it. The average age of death for these children is 13 years old. The 16 year old boy in Hamilton, Canada who is taking part in the medication research is responding to new drugs. He has gained weight, going from 24 to 31 pounds. The new drug called lonafarnib, was developed as a treatment for pediatric brain cancer but was proven to be ineffective for that disease. Now it has potential as a treatment for progeria, which is exacerbated by a build up of an abnormal protein, called progerin, said to accumulate in everyone as they age. The research into treating Progeria might also apply to other symptoms brought on by aging.